「Establishment of quantitative and consistent in vitro skeletal muscle pathological models of myotonic dystrophy type 1 using patient-derived iPSCs」の関連論文
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SMN promotes mitochondrial metabolic maturation during myogenesis by regulating the MYOD-miRNA axis
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Myogenetic oligodeoxynucleotide (myoDN) recovers the differentiation of skeletal muscle myoblasts deteriorated by diabetes mellitus.
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Mature Myotubes Generated From Human-Induced Pluripotent Stem Cells Without Forced Gene Expression
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Characterization of hiPSC-Derived Muscle Progenitors Reveals Distinctive Markers for Myogenic Cell Purification Toward Cell Therapy
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Simple derivation of skeletal muscle from human pluripotent stem cells using temperature‐sensitive Sendai virus vector
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Generation of macrophages with altered viral sensitivity from genome-edited rhesus macaque iPSCs to model human disease
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One-step induction of photoreceptor-like cells from human iPSCs by delivering transcription factors
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A muscle fatigue-like contractile decline was recapitulated using skeletal myotubes from Duchenne muscular dystrophy patient-derived iPSCs
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Cryptotanshinone is a candidate therapeutic agent for interstitial lung disease associated with a BRICHOS-domain mutation of SFTPC
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Myogenetic Oligodeoxynucleotide Induces Myocardial Differentiation of Murine Pluripotent Stem Cells
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ERRγ agonist under mechanical stretching manifests hypertrophic cardiomyopathy phenotypes of engineered cardiac tissue through maturation
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Human iPSC-derived renal collecting duct organoid model cystogenesis in ADPKD
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ERRγ enhances cardiac maturation with T-tubule formation in human iPSC-derived cardiomyocytes
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Differentiation of hypertrophic chondrocytes from human iPSCs for the in vitro modeling of chondrodysplasias
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N-Acetylcysteine prevents amyloid-β secretion in neurons derived from human pluripotent stem cells with trisomy 21
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Selective vulnerability of human-induced pluripotent stem cells to dihydroorotate dehydrogenase inhibition during mesenchymal stem/stromal cell purification
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Prophylactic treatment of rapamycin ameliorates naturally developing and episode -induced heterotopic ossification in mice expressing human mutant ACVR1
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Enhanced chondrogenic differentiation of iPS cell-derived mesenchymal stem/stromal cells via neural crest cell induction for hyaline cartilage repair
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Am80, a retinoic acid receptor agonist, activates the cardiomyocyte cell cycle and enhances engraftment in the heart
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Orai1–STIM1 Regulates Increased Ca²⁺ Mobilization, Leading to Contractile Duchenne Muscular Dystrophy Phenotypes in Patient-Derived Induced Pluripotent Stem Cells
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iPSC-derived type IV collagen α5-expressing kidney organoids model Alport syndrome
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Malfunctioning CD106-positive, short-term hematopoietic stem cells trigger diabetic neuropathy in mice by cell fusion.
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CDK8/19 inhibition plays an important role in pancreatic β-cell induction from human iPSCs
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The pluripotent stem cell-specific transcript ESRG is dispensable for human pluripotency
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Pluripotent stem cell model of Shwachman-Diamond syndrome reveals apoptotic predisposition of hemoangiogenic progenitors
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MYCL promotes iPSC-like colony formation via MYC Box 0 and 2 domains
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Myogenetic Oligodeoxynucleotide Restores Differentiation and Reverses Inflammation of Myoblasts Aggravated by Cancer-Conditioned Medium
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Azacitidine is a potential therapeutic drug for pyridoxine-refractory female X-linked sideroblastic anemia
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Generation of two human induced pluripotent stem cell lines derived from two X-linked adrenoleukodystrophy patients with ABCD1 mutations
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Enhancing the Therapeutic Efficacy of Bone Marrow-Derived Mononuclear Cells with Growth Factor-Expressing Mesenchymal Stem Cells for ALS in Mice.
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Collagen-VI supplementation by cell transplantation improves muscle regeneration in Ullrich congenital muscular dystrophy model mice
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Structurally-discovered KLF4 variants accelerate and stabilize reprogramming to pluripotency
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In vitro methods to ensure absence of residual undifferentiated human induced pluripotent stem cells intermingled in induced nephron progenitor cells
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Effect of prolonged culture and hypoxic conditions on in vitro neural differentiation potency of embryonic stem cell-derived neural stem cells
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Single-cell RNA-seq reveals heterogeneity in hiPSC-derived muscle progenitors and E2F family as a key regulator of proliferation
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Bone marrow-derived inducible microglia-like cells ameliorate motor function and survival in a mouse model of amyotrophic lateral sclerosis.
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Multi-omics approach reveals post-transcriptionally regulated genes are essential for human pluripotent stem cells
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Extracellular vesicles synchronize cellular phenotypes of differentiating cells
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iPS cells from Chediak-Higashi syndrome patients recapitulate the giant granules in myeloid cells
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Lionheart LincRNA alleviates cardiac systolic dysfunction under pressure overload
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Extracellular vesicles synchronize cellular phenotypes of differentiating cells
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Collagen X Is Dispensable for Hypertrophic Differentiation and Endochondral Ossification of Human iPSC-Derived Chondrocytes
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Expression dynamics of HAND1/2 in in vitro human cardiomyocyte differentiation
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A concise in vitro model for evaluating interactions between macrophage and skeletal muscle cells during muscle regeneration
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Transplantation of human iPSC-derived muscle stem cells in the diaphragm of Duchenne muscular dystrophy model mice
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Characterization and reduction of non-endocrine cells accompanying islet-like endocrine cells differentiated from human iPSC
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Constitutive activation of mTORC1 signaling induced by biallelic loss-of-function mutations in SZT2 underlies a discernible neurodevelopmental disease
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Gene Editing in Murine Hematopoietic Stem Cells Using a Novel Ex Vivo Expansion System
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Inhibition of cyclooxygenase-1 by nonsteroidal anti-inflammatory drugs demethylates MeR2 enhancer and promotes Mbnl1 transcription in myogenic cells
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Dual CRISPR-Cas3 system for inducing multi-exon skipping in DMD patient-derived iPSCs