「Low immunogenicity of LNP allows repeated administrations of CRISPR-Cas9 mRNA into skeletal muscle in mice」の関連論文
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Dual CRISPR-Cas3 system for inducing multi-exon skipping in DMD patient-derived iPSCs
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Efficient ssODN-Mediated Targeting by Avoiding Cellular Inhibitory RNAs through Precomplexed CRISPR-Cas9/sgRNA Ribonucleoprotein
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A muscle fatigue-like contractile decline was recapitulated using skeletal myotubes from Duchenne muscular dystrophy patient-derived iPSCs
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Extrahepatic gene delivery for cancer treatment and an investigation of factors that affect in vivo functional gene delivery [an abstract of entire text]
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Delivery of CRISPR-Cas tools for in vivo genome editing therapy: Trends and challenges
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Design and In vivo Evaluation of Novel mRNA Lipid Nanoparticles Beyond the Hepatocytes Towards a New Era of Personalized Gene Therapies [an abstract of entire text]
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Robust and efficient knock-in in embryonic stem cells and early-stage embryos of the common marmoset using the CRISPR-Cas9 system (本文)
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DIPA-CRISPR is a simple and accessible method for insect gene editing
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Transplantation of human iPSC-derived muscle stem cells in the diaphragm of Duchenne muscular dystrophy model mice
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Mature Myotubes Generated From Human-Induced Pluripotent Stem Cells Without Forced Gene Expression
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Cytosine base editing systems with minimized off-target effect and molecular size
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Design of Novel Targeted Co-delivery System for Combined Chemotherapy and Gene Therapy of Hepatocellular Carcinoma [an abstract of entire text]
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Gene Editing in Murine Hematopoietic Stem Cells Using a Novel Ex Vivo Expansion System
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Uniform transgene activation in Tet-On systems depends on sustained rtTA expression
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Optimized electroporation of CRISPR-Cas9/gRNA ribonucleoprotein complex for selection-free homologous recombination in human pluripotent stem cells
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MECHANISTIC ANALYSIS OF THE INITIATION OF RETROVIRAL GENE SILENCING BY REPROGRAMMING FACTORS
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One-step induction of photoreceptor-like cells from human iPSCs by delivering transcription factors
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Circulatory C-type natriuretic peptide reduces mucopolysaccharidosis-associated craniofacial hypoplasia in vivo
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In vivo regeneration of interspecies chimeric kidneys using a nephron progenitor cell replacement system
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Branchpoints as potential targets of exon-skipping therapies for genetic disorders
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Orthogonal Protein-Responsive mRNA Switches for Mammalian Synthetic Biology
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Chemical biology studies on nucleic acid recognition, modification, and secondary structures
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Gut contractile organoids: a novel model system to study the cellular synchronization in gastrointestinal motility
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Development and optimization of CRISPR-Cas9-based artificial transcription activator systems
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Development and optimization of CRISPR-Cas9-based artificial transcription activator systems
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Establishment of a heart‐on‐a‐chip microdevice based on human iPS cells for the evaluation of human heart tissue function
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Bioengineering and Cell-derived Strategies for Salivary Gland Regeneration
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Lionheart LincRNA alleviates cardiac systolic dysfunction under pressure overload
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Pluripotent stem cell-based therapies and their path to the clinic
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Establishment of quantitative and consistent in vitro skeletal muscle pathological models of myotonic dystrophy type 1 using patient-derived iPSCs
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シグナル伝達抗体(Signalobody)を用いた細胞の運命制御系の開発
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Improvement of mouse genome editing protocol and the application:investigation of the physiological roles of glycine receptor alpha 4 subunit.
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Generation of humanized liver in rats
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iPSC-derived type IV collagen α5-expressing kidney organoids model Alport syndrome
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Inhibition of cyclooxygenase-1 by nonsteroidal anti-inflammatory drugs demethylates MeR2 enhancer and promotes Mbnl1 transcription in myogenic cells
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Malfunctioning CD106-positive, short-term hematopoietic stem cells trigger diabetic neuropathy in mice by cell fusion.
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Generation of macrophages with altered viral sensitivity from genome-edited rhesus macaque iPSCs to model human disease
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A versatile and robust cell purification system with an RNA-only circuit composed of microRNA-responsive ON and OFF switches
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Programmable mammalian translational modulators by CRISPR-associated proteins
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Local application of Usag-1 siRNA can promote tooth regeneration in Runx2-deficient mice
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A new immunodeficient Duchenne muscular dystrophy rat model to evaluate engraftment after human cell transplantation
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De novo Selection of Macrocyclic Peptides Binding to TMEPAI family by Means of Random Non-standard Peptides Integrated Discovery System
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Systemic recombination in a novel Cre transgenic line, CAG-Cre C57BL/6N mouse
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Genome-scale CRISPR/Cas9 screening for gemcitabine modulators in pancreatic cancer
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A concise in vitro model for evaluating interactions between macrophage and skeletal muscle cells during muscle regeneration
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CRISPR/Cas9-mediated genome-edited mice reveal 10 testis-enriched genes are dispensable for male fecundity
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慢性炎症に対する免疫抑制の誘導のためのナノ粒子製剤の開発
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Structurally-discovered KLF4 variants accelerate and stabilize reprogramming to pluripotency
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Studies on Prediction of Cardiotoxicity Induced by Anticancer Drugs and Exploration of Molecular Targets to Prevent Cardiotoxicity
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Development of the first clinically used radiotracer [18F]T-401 for positron emission tomography imaging of monoacylglycerol lipase in brain (Monoacylglycerol lipase (MAGL)を標的としたPETトレーサー[18F]T-401の開発)