「Branchpoints as potential targets of exon-skipping therapies for genetic disorders」の関連論文
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MYCL promotes iPSC-like colony formation via MYC Box 0 and 2 domains
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Self-assembling small-molecule adjuvants as antigen nano-carriers
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Genome-wide CRISPR/Cas9 Screen for Porcine Epidemic Diarrhea Virus Resistance in Pig Intestinal Epithelial Cells
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DIPA-CRISPR is a simple and accessible method for insect gene editing
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Neuroinflammation in neurodegenerative disease
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主要組織適合遺伝子複合体および血清アルブミンに対するリガンド分子による薬物送達効率の改善戦略
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Inhibition of glycine cleavage system by pyridoxine 5'-phosphate causes synthetic lethality in glyA yggS and serA yggS in Escherichia coli
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Osteogenic cocktail induces calcifications in human breast cancer cell line via placental alkaline phosphatase expression.
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Comprehensive behavioral analysis of the mice deficient in Akain1, a novel protein kinase A-binding protein.
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Development of a 1:1-binding biparatopic anti-TNFR2 antagonist by reducing signaling activity through epitope selection
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Inherent genomic properties underlie the epigenomic heterogeneity of human induced pluripotent stem cells
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Atypical protein kinase C iota (PKCλ/ι) ensures mammalian development by establishing the maternal-fetal exchange interface.
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アミノ酸およびペプチドによる食中毒細菌の生存とバイオフィルム形成の制御
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Congenital goitrous hypothyroidism is caused by dysfunction of the iodide transporter SLC26A7
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CDK8/19 inhibition plays an important role in pancreatic β-cell induction from human iPSCs
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Concepts of Regeneration for Spinal Diseases in 2021
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Study on Immunological Detection of Swine Influenza Virus Using Rabbit Monoclonal Antibody
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Analyses of the Molecular Determinant of Cell Fate Induced by an Antimetabolite, Trifluridine
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The mechanism of action of Spi-B in the transcriptional activation of the interferon-α4 gene
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FGF5 and EPAS1 gene polymorphisms are associated with high-altitude adaptation in Nepalese goat breeds
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A drug repurposing study based on clinical big data for the protective role of vitamin D in olanzapine-induced dyslipidemia
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Genome-wide association study and HLA fine-mapping for childhood steroid-sensitive nephrotic syndrome in the Japanese population
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Beta-1,4-galactosyltransferase-3 deficiency suppresses the growth of immunogenic tumors in mice
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Structural and biochemical study on the dual coenzyme (NADP+/NAD+) specific isocitrate dehydrogenase from Trypanosoma brucei glycosome
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A protocol to construct RNA-protein devices for photochemical translational regulation of synthetic mRNAs in mammalian cells
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The Roles of Cancer-Associated Fibroblasts in Colorectal Carcinogenesis
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Exacerbation of epilepsy by astrocyte alkalization and gap junction uncoupling.
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Development studies based on Kampo theories for new treatment strategies and drug discoveries
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Functional rejuvenation of aged neural stem cells by Plagl2 and anti-Dyrk1a activity
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Detection of Acinetobacter pittii ST220 co-producing NDM-1 and OXA-820 carbapenemases from a hospital sink in a non-endemic country of NDM
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CD44v9 Induces Stem Cell-Like Phenotypes in Human Cholangiocarcinoma
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The mechanistic role of fatty acid binding protein 7 (FABP7) in tumor proliferation
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In silico study of RNA-seq and H3 Trimethylation ChIP-seq analysis in combination with laser-microdissection on human lung cancer cells
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Secretion of signal peptides via extracellular vesicles
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C type natriuretic peptide facilitates autonomous Ca²⁺ entry in growth plate chondrocytes for stimulating bone growth
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Systematic chemical screening identifies disulfiram as a repurposed drug that enhances sensitivity to cisplatin in bladder cancer: a summary of preclinical studies
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Myosin heavy chain, a novel allergen for fish allergy in patients with atopic dermatitis
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Studies on the roles of EMT-associated microRNAs in cervical cancer and aggressive endometrial cancer
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The Effect of Ethanol on Disassembly of Amyloid-β1-42 Pentamer Revealed by Atomic Force Microscopy and Gel Electrophoresis.
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Evolutional transition of HBV genome during the persistent infection determined by single-molecule real-time sequencing
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Thiopurine Use During Pregnancy Has Deleterious Effects on Offspring in Nudt15 R138C Knock-In Mice.
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Amplified EPOR/JAK2 Genes Define a Unique Subtype of Acute Erythroid Leukemia
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Postoperative supraventricular tachycardia and polymorphic ventricular tachycardia due to a novel SCN5A variant: a case report of a rare comorbidity that is difficult to diagnose.
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Study on chemical compounds for the development of anti-ebolavirus drugs [an abstract of entire text]
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Combination of RERG and ZNF671 methylation rates in circulating cell-free DNA: A novel biomarker for screening of nasopharyngeal carcinoma
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Transplantation of human iPSC-derived muscle stem cells in the diaphragm of Duchenne muscular dystrophy model mice
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Acute inhibition of AMPA receptors by perampanel reduces amyloid β-protein levels by suppressing β-cleavage of APP in Alzheimer's disease models
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The mechanism of myosin replacement in the thick filament of the skeletal muscle [an abstract of entire text]
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Molecular basis of lipid presenting and loading mechanisms of CD1b [an abstract of entire text]
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Automated amplification-free digital RNA detection platform for rapid and sensitive SARS-CoV-2 diagnosis