「Branchpoints as potential targets of exon-skipping therapies for genetic disorders」の関連論文
-
Studies on the Transport Mechanism and Physiological Roles of a Cargo Protein of Extracellular Membrane Vesicles from Shewanella vesiculosa HM13
-
A disease-specific iPS cell resource for studying rare and intractable diseases
-
A type 2C protein phosphatase activates high-affinity nitrate uptake by dephosphorylating NRT2.1
-
The relationship between DRD2 Taq1A polymorphism and white matter structure in healthy young adults.
-
Myogenetic Oligodeoxynucleotides as Anti-Nucleolin Aptamers Inhibit the Growth of Embryonal Rhabdomyosarcoma Cells
-
Identification of Virus Receptors
-
Monitoring mitochondrial translation by pulse SILAC
-
Olfactory marker protein is unlikely to be cleaved by calpain 5
-
Role of carbonic anhydrases in ferroptosis-resistance
-
Hippo-TAZ signaling is the master regulator of the onset of triple-negative basal-like breast cancers
-
Establishment of a mouse model of troglitazone-induced liver injury and analysis of its hepatotoxic mechanism
-
Glucose transporter Glut1 controls diffuse invasion phenotype with perineuronal satellitosis in diffuse glioma microenvironment
-
S-1-Propenylcysteine promotes IL-10-induced M2c macrophage polarization through prolonged activation of IL-10R/STAT3 signaling
-
S-1-Propenylcysteine promotes IL-10-induced M2c macrophage polarization through prolonged activation of IL-10R/STAT3 signaling
-
Design, synthesis, and evaluation of fluorogenic cyanine dyes for nucleolar RNA imaging in living cells: effect of regioisomers on probe functions
-
Study on the regulation of CD8+ T cell immune response through nuclear receptor RORα and REV-ERB [an abstract of entire text]
-
Forced expression of α2,3-sialyltransferase IV rescues impaired heart development in α2,6-sialyltransferase I-deficient medaka
-
ATM suppresses c-Myc overexpression in the mammary epithelium in response to estrogen
-
Sarcomatoid mesothelioma diagnosed in a patient with mesothelioma in situ: a case report on morphologic differences after 9-month interval with details analysis of cytology in early-stage mesothelioma
-
Establishment and Application of Anti-CD20 Monoclonal Antibodies using the Cell-based Immunization and Screening Method for the Detection of B Cells
-
Re-generation of cytotoxic γδT cells with distinctive signatures from human γδT-derived iPSCs
-
Studies on Unusual Oxidative Transformations in Fungal Natural Product Biosynthesis [an abstract of entire text]
-
Clinical Significance of Serum Galectin-9 and Soluble CD155 Levels in Patients with Systemic Sclerosis
-
Myh9 R702C is associated with erythroid abnormality with splenomegaly in mice
-
Development of macrophage-targeted therapy using peptide/protein-loaded extracellular vesicles
-
Primordial germ cell-specific expression of eGFP in transgenic chickens
-
Structure-based screening combined with computational and biochemical analyses identified the inhibitor targeting the binding of DNA Ligase 1 to UHRF1
-
Fruit Fly, Drosophila melanogaster, as an In Vivo Tool to Study the Biological Effects of Proton Irradiation
-
Study on serological diagnostic assays for Crimean-Congo hemorrhagic fever
-
Eighteen-years follow-up of congenital hypothyroidism by TSHR gene p.Arg109Gln and p.Arg450His variants
-
Delivery of CRISPR-Cas tools for in vivo genome editing therapy: Trends and challenges
-
An Isoform-Selective Modulator of Cryptochrome 1 Regulates Circadian Rhythms in Mammals
-
Cutaneous Liver X Receptor Activation Prevents the Formation of Imiquimod-Induced Psoriatic Dermatitis
-
MYC Upregulation Is a Useful Biomarker for Preoperative Neoadjuvant Chemotherapy Combined With Anti-EGFR in Liver Metastasis from Colorectal Cancer
-
ベンジルイソキノリンアルカロイド、ヒゲナミンおよびベルベリン検出のためのバイオアッセイの開発
-
RIL-StEp: epistasis analysis of rice recombinant inbred lines (RILs) reveals candidate interacting genes that control seed hull color and leaf chlorophyll content
-
Urinary MicroRNA-Based Diagnostic Model for Central Nervous System Tumors Using Nanowire Scaffolds
-
RNA Sequencing of Medusavirus Suggests Remodeling of the Host Nuclear Environment at an Early Infection Stage
-
Tumor elimination by clustered microRNAs miR-306 and miR-79 via noncanonical activation of JNK signaling
-
Role of Persulfides/Polysulfides in Reversibility of S-Oxidation of Sensor Proteins during Oxidative Stress
-
Gpr19 is a circadian clock-controlled orphan GPCR with a role in modulating free-running period and light resetting capacity of the circadian clock
-
Long-read bitter gourd (Momordica charantia) genome and the genomic architecture of nonclassic domestication
-
Profiling of Naquotinib, a Small Molecule Kinase Inhibitor, as EGFR and BTK Inhibitor
-
Clinical characteristics of Corynebacterium simulans
-
An Integrated In Silico and In Vivo Approach to Identify Protective Effects of Palonosetron in Cisplatin-Induced Nephrotoxicity
-
高度好熱性真正細菌Thermotoga maritimaの複製起点における開始複合体の形成メカニズムと開裂部位の特性の解析
-
Decreased serum phosphate levels are a useful biomarker to predict occurrence and severity of cytokine release syndrome in chimeric antigen receptor T-cell therapy
-
Nucleolar stress: Molecular mechanisms and related human diseases
-
Repurposing bromocriptine for Aβ metabolism in Alzheimer’s disease (REBRAnD) study: randomised placebo-controlled double-blind comparative trial and open-label extension trial to investigate the safety and efficacy of bromocriptine in Alzheimer’s disease with presenilin 1 (PSEN1) mutations
-
Safety comparisons among monoamine oxidase inhibitors against Parkinson’s disease using FDA adverse event reporting system