「Dual CRISPR-Cas3 system for inducing multi-exon skipping in DMD patient-derived iPSCs」の関連論文
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In vitro methods to ensure absence of residual undifferentiated human induced pluripotent stem cells intermingled in induced nephron progenitor cells
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Development of nucleic acid therapeutics based on the control of their intracellular distribution
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Functional studies of the egg cortical alveolus proteases on fertilization of medaka
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Combination of tumor necrosis factor-α and epidermal growth factor induces the adrenergic-to-mesenchymal transdifferentiation in SH-SY5Y neuroblastoma cells
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Discovery of Non-Cysteine-Targeting Covalent Inhibitors by Activity-Based Proteomic Screening with a Cysteine-Reactive Probe
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TEAD1 trapping by the Q353R–Lamin A/C causes dilated cardiomyopathy
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Variation of body weight and seasonal reproduction in populations from different latitudes: genetic analyses using wild-derived medaka fish
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An ancient retroviral RNA element hidden in mammalian genomes and its involvement in co-opted retroviral gene regulation
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Discovery and biological significance of the sialate:O-sulfotransferases in vertebrates
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Generation and evaluation of a transgenic zebrafish for tissue-specific expression of a dominant-negative Rho-associated protein kinase-2
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Comprehensive genomics in androgen receptor-dependent castration-resistant prostate cancer identifies an adaptation pathway mediated by opioid receptor kappa 1
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iPSC-derived type IV collagen α5-expressing kidney organoids model Alport syndrome
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Non–redundancy of Rice Mutant Library for Male Gametogenesis Confirmed by Bulked Segregants Analysis Using Illumina BeadsArray
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Monitoring mitochondrial translation by pulse SILAC
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Production of IgG1-based bispecific antibody without extra cysteine residue via intein-mediated protein trans-splicing.
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Identification of PTPRσ-interacting proteins by proximity-labelling assay
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Stability and Oligomerization of Mutated SMN Protein Determine Clinical Severity of Spinal Muscular Atrophy
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Downregulation of lncRNA PVT1 inhibits proliferation and migration of mesothelioma cells by targeting FOXM1
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Downregulation of lncRNA PVT1 inhibits proliferation and migration of mesothelioma cells by targeting FOXM1
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Neural Isoforms of Agrin Are Generated by Reduced PTBP1−RNA Interaction Network Spanning the Neuron−Specific Splicing Regions in AGRN
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Conformational change of RNA‐helicase DHX30 by ALS/FTD‐linked FUS induces mitochondrial dysfunction and cytosolic aggregates
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Establishment of quantitative and consistent in vitro skeletal muscle pathological models of myotonic dystrophy type 1 using patient-derived iPSCs
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Development of antisense oligonucleotides for suppressing breast cancer cell proliferation and the system for evaluating drug response of cardiomyocytes
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Mechanism-Based Personalized Medicine for Cystic Fibrosis by Suppressing Pseudo Exon Inclusion
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Application of Advanced Genomic Technology to Improve Timber Productivity and Wood Quality of a Commercial Timber Species in Tropical Rainforest
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Versatile strategy using vaccinia virus-capping enzyme to synthesize functional 5′ cap-modified mRNAs
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Development of thiazole orange-carrying peptide nucleic acid small molecule conjugate probes for the promoter region of Influenza A virus
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Next Generation Sequencing-Based Transcriptome Predicts Bevacizumab Efficacy in Combination with Temozolomide in Glioblastoma
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A digital twin reproducing gene regulatory network dynamics of early Ciona embryos indicates robust buffers in the network
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DNA methyltransferase 3B plays a protective role against hepatocarcinogenesis caused by chronic inflammation via maintaining mitochondrial homeostasis
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Engineered fast-dissociating antibody fragments for multiplexed super-resolution microscopy
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Development of genetic management methods for rice varieties and prediction of spontaneous mutation frequencies using next-generation sequencing technology [an abstract of entire text]
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Generation of two human induced pluripotent stem cell lines derived from two X-linked adrenoleukodystrophy patients with ABCD1 mutations
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Circulatory C-type natriuretic peptide reduces mucopolysaccharidosis-associated craniofacial hypoplasia in vivo
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6. Life Science and Medical Science
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Gene Deletion Algorithms for Minimum Reaction Network Design by Mixed-Integer Linear Programming for Metabolite Production in Constraint-Based Models: gDel_minRN
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Characterization of the Anticancer Activities of Some Natural and Synthetic Compounds: Molecular Targets and Mechanism
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The role of H3K27 demethylation in retinal development
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Enhancement of Vivid-based photo-activatable Gal4 transcription factor in mammalian cells
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Cryptic insertion of CBFB into MYH11 leading to a type D fusion in acute myeloid leukemia with normal karyotype
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Inhibition of heat shock protein 90 destabilizes receptor tyrosine kinase ROR1 in lung adenocarcinoma
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A RUNX-targeted gene switch-off approach modulates the BIRC5/PIF1-p21 pathway and reduces glioblastoma growth in mice
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MicroRNA-124a Inhibits Endoderm Lineage Commitment in Mouse Embryonic Stem Cells
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The role of GPNMB ectodomain in breast cancer development
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PML-RARαはMED1との結合を介して全トランス型レチノイン酸依存性の転写活性化を誘導する
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An old model with new insights: endogenous retroviruses drive the evolvement toward ASD susceptibility and hijack transcription machinery during development
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Analyses of genetic and retinal lesions in Ccdc85c knockout rats: a rat model of genetic hydrocephalus
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Production and characterization of monoclonal antibodies specific for major capsid VP1 protein of trichodysplasia spinulosa-associated polyomavirus
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Bioengineering and Cell-derived Strategies for Salivary Gland Regeneration
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Mouse Slfn8 and Slfn9 genes complement human cells lacking SLFN11 during the replication stress response