「Dual CRISPR-Cas3 system for inducing multi-exon skipping in DMD patient-derived iPSCs」の関連論文
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Efficient ssODN-Mediated Targeting by Avoiding Cellular Inhibitory RNAs through Precomplexed CRISPR-Cas9/sgRNA Ribonucleoprotein
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Robust and efficient knock-in in embryonic stem cells and early-stage embryos of the common marmoset using the CRISPR-Cas9 system (本文)
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Low immunogenicity of LNP allows repeated administrations of CRISPR-Cas9 mRNA into skeletal muscle in mice
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Branchpoints as potential targets of exon-skipping therapies for genetic disorders
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Cytosine base editing systems with minimized off-target effect and molecular size
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Development and optimization of CRISPR-Cas9-based artificial transcription activator systems
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Development and optimization of CRISPR-Cas9-based artificial transcription activator systems
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MECHANISTIC ANALYSIS OF THE INITIATION OF RETROVIRAL GENE SILENCING BY REPROGRAMMING FACTORS
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Chemical biology studies on nucleic acid recognition, modification, and secondary structures
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Uniform transgene activation in Tet-On systems depends on sustained rtTA expression
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Orthogonal Protein-Responsive mRNA Switches for Mammalian Synthetic Biology
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All reported non-canonical splice site variants in GLA cause aberrant splicing
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One-step induction of photoreceptor-like cells from human iPSCs by delivering transcription factors
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DIPA-CRISPR is a simple and accessible method for insect gene editing
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Programmable mammalian translational modulators by CRISPR-associated proteins
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A pipeline for complete characterization of complex germline rearrangements from long DNA reads
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Usefulness of functional splicing analysis to confirm precise disease pathogenesis in Diamond-Blackfan anemia caused by intronic variants in RPS19
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Quick and affordable DNA cloning by reconstitution of Seamless Ligation Cloning Extract using defined factors
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Target-dependent RNA polymerase as universal platform for gene expression control in response to intracellular molecules
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Marker-free genome editing in the edible mushroom, Pleurotus ostreatus, using transient expression of genes required for CRISPR/Cas9 and for selection
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Studies on identification and evaluation of CRISPR diversity on human skin microbiome for development of a new personal identification method
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Gene Editing in Murine Hematopoietic Stem Cells Using a Novel Ex Vivo Expansion System
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Functional and genomic characterization of patient-derived xenograft model to study adaptation to mTORC1 inhibitor in clear cell renal cell carcinoma
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Long-Read Sequence Confirmed a Large Deletion Including MYH6 and MYH7 in an Infant of Atrial Septal Defect and Atrial Arrhythmias.
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Biomolecular nanotechnology-based approaches to investigate nucleic acid interactions
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Identification of calcium and integrin-binding protein 1 (CIB1) as a novel regulator of production of Amyloid β peptide using CRISPR/Cas9-based screening system
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Lionheart LincRNA alleviates cardiac systolic dysfunction under pressure overload
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Molecular Mechanism of Quinclorac Resistance in Multiple-Herbicide Resistant Echinochloa phyllopogon
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Hamster PIWI proteins bind to piRNAs with stage-specific size variations during oocyte maturation (本文)
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Transposon delivery for CRISPR-based loss-of-function screen in mice identifies NF2 as a cooperating gene involved with the canonical WNT signaling molecular class of hepatocellular carcinoma
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A versatile and robust cell purification system with an RNA-only circuit composed of microRNA-responsive ON and OFF switches
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Delivery of CRISPR-Cas tools for in vivo genome editing therapy: Trends and challenges
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Genome-wide profiling of histone H3K4me3 and H3K27me3 modifications in individual blastocysts by CUT&Tag without a solid support (NON-TiE-UP CUT&Tag)
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An ancient retroviral RNA element hidden in mammalian genomes and its involvement in co-opted retroviral gene regulation
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Extrahepatic gene delivery for cancer treatment and an investigation of factors that affect in vivo functional gene delivery [an abstract of entire text]
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Genome-scale CRISPR/Cas9 screening for gemcitabine modulators in pancreatic cancer
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Mature Myotubes Generated From Human-Induced Pluripotent Stem Cells Without Forced Gene Expression
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Design and In vivo Evaluation of Novel mRNA Lipid Nanoparticles Beyond the Hepatocytes Towards a New Era of Personalized Gene Therapies [an abstract of entire text]
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Genetic and Physiological Characterization of Tomato F-box Gene HAWAIIAN SKIRT Mutants
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Analysis of disease model iPSCs derived from patients with a novel Fanconi anemia-like IBMFS ADH5/ALDH2 deficiency
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Optimized electroporation of CRISPR-Cas9/gRNA ribonucleoprotein complex for selection-free homologous recombination in human pluripotent stem cells
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Studies on multifunctional genome elements functioning in mouse spermatogenesis [an abstract of entire text]
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Comprehensive analysis of full-length transcripts reveals novel splicing abnormalities and oncogenic transcripts in liver cancer
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A two-step screening to optimize the signal response of an auto-fluorescent protein-based biosensor
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Generation of macrophages with altered viral sensitivity from genome-edited rhesus macaque iPSCs to model human disease
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Clinical impact of detecting low-frequency variants in cell-free DNA on treatment of castration-resistant prostate cancer
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Identification and analysis of mechanisms that bypass the essentiality of Polo, a mitotic regulator
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De novo Selection of Macrocyclic Peptides Binding to TMEPAI family by Means of Random Non-standard Peptides Integrated Discovery System
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Study on Accessory Gene Regulator(AGR)Variants in Staphylococcus aureus
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Comprehensive analysis of TCR function using a novel system reveals the multiple unconventional tumor-reactive T cells in breast cancer-infiltrating lymphocytes