「Dual CRISPR-Cas3 system for inducing multi-exon skipping in DMD patient-derived iPSCs」の関連論文
-
ReCGBM: a gradient boosting-based method for predicting human dicer cleavage sites
-
Edge-localized alteration in pluripotency state of mouse ES cells forming topography-confined layers on designed mesh substrates
-
Long-Surviving Adult Siblings With Joubert Syndrome Harboring a Novel Compound Heterozygous CPLANE1 Variant
-
In situ vaccination using unique TLR9 ligand K3-SPG induces long-lasting systemic immune response and synergizes with systemic and local immunotherapy
-
Reproducible production and image-based quality evaluation of retinal pigment epithelium sheets from human induced pluripotent stem cells
-
Speciation in the Patelloida saccharina species complex across the Japanese Archipelago
-
Biochemical and structural investigation of NPM1-mediated liquid-liquid phase separation in Adenovirus infection
-
Molecular genetic study of the FMR1 CGG repeat configurations in the Japanese population and patients with Fragile X-Associated Tremor/Ataxia Syndrome
-
Comprehensive behavioral analysis of the mice deficient in Akain1, a novel protein kinase A-binding protein.
-
Target Identification Using Homopharma and Network-Based Methods for Predicting Compounds Against Dengue Virus-Infected Cells
-
Elucidating the Micronuclear Functions in the Central Nervous System
-
Self-assembling small-molecule adjuvants as antigen nano-carriers
-
Development studies based on Kampo theories for new treatment strategies and drug discoveries
-
miR-142 induces accumulation of reactive oxygen species (ROS) by inhibiting pexophagy in aged bone marrow mesenchymal stem cells
-
Efficacy of the Novel Tubulin Polymerization Inhibitor PTC-028 for Myelodysplastic Syndrome
-
Study on the role of zona pellucida in pre- and post-implantation development of mouse embryos [an abstract of entire text]
-
Inhibition of microRNA-33b specifically ameliorates abdominal aortic aneurysm formation via suppression of inflammatory pathways
-
A Single RET Mutation in Hirschsprung Disease Induces Intestinal Aganglionosis Via a Dominant-Negative Mechanism
-
Studies on Prediction of Cardiotoxicity Induced by Anticancer Drugs and Exploration of Molecular Targets to Prevent Cardiotoxicity
-
Simple derivation of skeletal muscle from human pluripotent stem cells using temperature‐sensitive Sendai virus vector
-
Development of the first clinically used radiotracer [18F]T-401 for positron emission tomography imaging of monoacylglycerol lipase in brain (Monoacylglycerol lipase (MAGL)を標的としたPETトレーサー[18F]T-401の開発)
-
Genomic analysis of multiple myeloma using targeted capture sequencing in the Japanese cohort
-
Structural insights into tetraspanin CD9 function
-
Recursive Vesicle Reproduction System Coupled with Enzymatic Cascade Reactions: Toward Synthetic Minimal Cell
-
Combined landscape of single-nucleotide variants and copy number alterations in clonal hematopoiesis
-
Distinct but interchangeable subpopulations of colorectal cancer cells with different growth fates and drug sensitivity
-
Population Dynamics in the Biogenesis of Single-/Multi-Layered Membrane Vesicles Revealed by Encapsulated GFP-Monitoring Analysis
-
Studies on Thermoregulation and Growth Performance in Chicks with av-UCP mutation
-
Studies on the Transport Mechanism and Physiological Roles of a Cargo Protein of Extracellular Membrane Vesicles from Shewanella vesiculosa HM13
-
Analyses of the Molecular Determinant of Cell Fate Induced by an Antimetabolite, Trifluridine
-
Extracellular vesicles synchronize cellular phenotypes of differentiating cells
-
DMRT1-mediated reprogramming drives development of cancer resembling human germ cell tumors with features of totipotency
-
MYCL promotes iPSC-like colony formation via MYC Box 0 and 2 domains
-
Fluid flow-induced left-right asymmetric decay of Dand5 mRNA in the mouse embryo requires a Bicc1-Ccr4 RNA degradation complex
-
Grafting Hydrophobic Amino Acids Critical for Inhibition of Protein–Protein Interactions on a Cell-Penetrating Peptide Scaffold
-
A cerebrospinal fluid microRNA analysis: Progressive supranuclear palsy
-
ERRγ enhances cardiac maturation with T-tubule formation in human iPSC-derived cardiomyocytes
-
Genomics-based discrimination of 2n gamete formation mechanisms in polyploids: a case study in nonaploid Diospyros kaki ‘Akiou’
-
Orai1–STIM1 Regulates Increased Ca²⁺ Mobilization, Leading to Contractile Duchenne Muscular Dystrophy Phenotypes in Patient-Derived Induced Pluripotent Stem Cells
-
A novel graph convolutional neural network for predicting interaction sites on protein kinase inhibitors in phosphorylation
-
Mechanisms of HIV-induced peripheral neuropathic pain by focusing on Schwann cell-macrophage interaction
-
GSK3 inhibitor enhances gemtuzumab ozogamicin-induced apoptosis in primary human leukemia cells by overcoming multiple mechanisms of resistance
-
l-Asparaginase regulates mTORC1 activity via a TSC2-dependent pathway in pancreatic beta cells
-
Prognostic stratification for IDH-wild-type lower-grade astrocytoma by Sanger sequencing and copy-number alteration analysis with MLPA
-
Understanding the role of de novo tracheary elements in Nicotiana interfamily grafting
-
Characterization of FLOWERING LOCUS C 5 in Brassica rapa L.
-
Combination of RERG and ZNF671 methylation rates in circulating cell-free DNA: A novel biomarker for screening of nasopharyngeal carcinoma
-
Study of the Effects of Inhibition of Epigenetic Regulators on the Proliferation of Hematological Malignant Tumor Cells
-
A study on the immunostimulatory effects of alarmin HMGN1 in cancer immunity
-
2-nitroimidazoles induce mitochondrial stress and ferroptosis in glioma stem cells residing in a hypoxic niche (本文)